Aragon-Gawinska, K, Seferian, AM, Daron, A, Gargaun, E, Vuillerot, C, Cances, C, Nusinersen in patients older than 7 months with spinal muscular atrophy type 1: A cohort study (2018) Neurology, 91, pp. e1312-e1318
Mercuri, E, Darras, BT, Chiriboga, CA, Chiriboga, A, Day, JW, Campbell, C, Nusinersen versus sham control in later-onset spinal muscular atrophy (2018) N Engl J Med, 378, pp. 625-635
Dangouloff, T, Servais, L., Clinical Evidence Supporting Early Treatment Of Patients With Spinal Muscular Atrophy: Current Perspectives (2019) Ther Clin Risk Manag, 15, pp. 1153-1161
Mendell, JR, Al-Zaidy, S, Shell, R, Arnold, WD, Rodino-Klapac, LR., Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy (2017) N Engl J Med, 377, pp. 1713-1722
Boemer, F, Caberg, JH, Dideberg, V, Beckers, P, Marie, S, Marcelis, L, (S)un (M)ay (A)rise on SMA: the hope of a region without spinal muscular atrophy (2019) Rev Méd Liege, 74, pp. 461-464
Boemer, F, Caberg, JH, Dideberg, V, Dardenne, D, Bours, V, Hiligsmann, M, Newborn screening for SMA in Southern Belgium (2019) Neuromuscul Disord, 29, pp. 343-349