Article (Scientific journals)
Randomisation versus prioritisation in a managed access programme: Lessons from spinal muscular atrophy.
Servais, Laurent; Kirschner, Janbernd; Muntoni, Francesco
2020In Neuromuscular disorders : NMD, 30 (4), p. 267-269
 

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Keywords :
Ethics; Gene therapy; Managed access programme; Spinal Muscular Atrophy; Treatment
Disciplines :
Pediatrics
Neurology
Author, co-author :
Servais, Laurent ;  Université de Liège - ULiège > Département des sciences cliniques > Département des sciences cliniques
Kirschner, Janbernd
Muntoni, Francesco
Language :
English
Title :
Randomisation versus prioritisation in a managed access programme: Lessons from spinal muscular atrophy.
Publication date :
April 2020
Journal title :
Neuromuscular disorders : NMD
ISSN :
0960-8966
eISSN :
1873-2364
Volume :
30
Issue :
4
Pages :
267-269
Commentary :
doi: 10.1016/j.nmd.2020.03.006. Epub 2020 Apr 17
Available on ORBi :
since 01 February 2021

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