Sansone, V. A., Walter, M. C., Attarian, S., DELSTANCHE, S., Mercuri, E., Lochmüller, H., Neuwirth, C., Vazquez-Costa, J. F., Kleinschnitz, C., & Hagenacker, T. (2020). Measuring Outcomes in Adults with Spinal Muscular Atrophy - Challenges and Future Directions - Meeting Report.
Journal of Neuromuscular Diseases, 7 (4), 523 - 534. doi:10.3233/JND-200534
https://hdl.handle.net/2268/334255